ГоловнаArchive of numbers2019Volume 27, issue 3 (100) Analysis of medical aid in patients with Duchenne muscular dystrophy, seven years’ dynamics
Title of the article Analysis of medical aid in patients with Duchenne muscular dystrophy, seven years’ dynamics
Authors Shatillo Andrii
Fedorenko Hanna
In the section The Scientifi c and Practical Conference proceedings "Modern Approaches to the Diagnosis and Treatment of Nervous System Diseases in Children", September 19—20, Kharkiv
Year 2019 Issue Volume 27, issue 3 (100) Pages 97-100
Type of article Scientific article Index UDK 616-007.17:616.74-008 Index BBK -
Abstract The article represents analysis of current practice of medical aid in Duchenne muscular dystrophy (DMD) patients in Ukraine through its compliance to international consensus. DMD is disease, which is related to type of rare ones, it has fatal course and leads to death at the age about twenty years. However, recent abilities of medical management substantially increase periods of good functioning and entire life expectancy. Analysis has been made on data from Ukrainian DMD registry. 75 entries from the registry were selected on basis of data completeness and consistency. Improvements of corticosteroid therapy prevalence and age of diagnosis, compared to 2012 indexes, have been revealed. Most diffi cult problem, which does not have visible progress, is equipment (motorized chairs, cough assist machines, BIBAP-machines) supply. It is noticed that along with widening of specific to DMD children medical aid, number of wrong or inadequate recommendations has been increased. Possibility of medical aid improvement for patients with DMD or similar rare conditions by the help of “centers of expertize” has been discussed.
Key words Duchenne muscular dystrophy, DMD, Ukrainian DMD registry, medical management, analisys
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